Roche Pauses Commercial and Clinical Use of Elevidys After Fatal Liver Failures
Roche discontinued the commercial and clinical use of Elevidys after two cases of fatal acute liver failure.
The Swiss pharmaceutical company said Sunday that the dosing of non-ambulatory patients, irrespective of their age, is paused in the clinical setting with immediate effect. Enrolment and dosing of non-ambulatory patients will also be immediately paused until additional risk mitigation measures are implemented, it added. Meanwhile, non-ambulatory patients shouldn't receive Elevidys in commercial settings.
Hashtags
Try Our AI Features
Explore what Daily8 AI can do for you:
Comments
No comments yet...
Related Articles
Yahoo
29 minutes ago
- Yahoo
Piper Sandler Reaffirms Overweight Rating on Soleno (SLNO) Driven by Strong VYKAT XR Prospects
Soleno Therapeutics Inc. (NASDAQ:SLNO) is one of the 10 biotech stocks screaming a buy now. On June 17, Piper Sandler reiterated an 'Overweight' rating on the stock with a $145 price target. The bullish stance follows positive discussions with a European specialist on the company's VYKAT XR medication for Prader-Willi syndrome (PWS). A scientist in a laboratory examining a microscope in the pursuit of cell therapy discoveries. Piper Sandler consulted a UK-based pediatric endocrinologist to understand the drug better. The specialist indicated she would prescribe the drug as medication for Prader-Willi syndrome (PWS) to all eligible patients upon approval. Soleno Therapeutics' edge with the drug stems from the fact that other PWS treatments are in the early stages of development. Piper Sandler believes VYKAT XT represents significant potential as the first approved treatment specifically addressing PWS, a condition. The biotech company plans to file a Marketing Authorization Application for VYKAT XR in the second quarter. It's also pursuing regulatory approval in Europe as it plans to fill with the European Medicines agency. Following regulatory approvals, Soleno Therapeutics Palms will launch the drug in the first quarter of 2026. Soleno Therapeutics is a biopharmaceutical company that develops and commercializes novel treatments for rare diseases. Their lead product, diazoxide choline extended-release tablets (DCCR), is being developed for Prader-Willi syndrome (PWS), specifically to address hyperphagia (excessive hunger). While we acknowledge the potential of SLNO as an investment, we believe certain AI stocks offer greater upside potential and carry less downside risk. If you're looking for an extremely undervalued AI stock that also stands to benefit significantly from Trump-era tariffs and the onshoring trend, see our free report on the best short-term AI stock. READ NEXT: 13 Best Software Stocks to Buy Now and 11 Must-Buy AI Stocks Analysts Are Betting On. Disclosure: None. Error in retrieving data Sign in to access your portfolio Error in retrieving data Error in retrieving data Error in retrieving data Error in retrieving data
Yahoo
29 minutes ago
- Yahoo
Acadia Pharmaceuticals (ACAD) Conducts Inducement Awards to Attract and Retain Top Talent
ACADIA Pharmaceuticals Inc. (NASDAQ:ACAD) is one of the 10 biotech stocks screaming a buy. On June 17, the company moved to attract and retain top talent by granting inducement awards to 41 employees. Under the 2024 Inducement Plan, the company will award the employees non-qualified stock options of 187,664 shares and 89.582 restricted stock units designed to attract and retain talent. A pharmacist in a pharmacy preparing a prescription medication for a patient suffering from Fibromyalgia. The move to offer inducement awards is part of Acadia Pharmaceuticals' push to secure top-skilled professionals essential for its neuroscience projects. It expects the awards to ensure employees are incentivized to contribute to the long-term objectives expected to lead to sustained growth and innovation. ACADIA Pharmaceuticals Inc. (NASDAQ:ACAD) is a biopharma company dedicated to advancing treatments for central nervous system disorders and rare diseases. Its key products include NUPLAZID, approved for Parkinson's disease psychosis, and DAYBUE. While we acknowledge the potential of ACAD as an investment, we believe certain AI stocks offer greater upside potential and carry less downside risk. If you're looking for an extremely undervalued AI stock that also stands to benefit significantly from Trump-era tariffs and the onshoring trend, see our free report on the best short-term AI stock. READ NEXT: 13 Best Software Stocks to Buy Now and 11 Must-Buy AI Stocks Analysts Are Betting On. Disclosure: None. 擷取數據時發生錯誤 登入存取你的投資組合 擷取數據時發生錯誤 擷取數據時發生錯誤 擷取數據時發生錯誤 擷取數據時發生錯誤
Yahoo
2 hours ago
- Yahoo
Health care workers on alert for ICE raids in hospitals
President Trump's whittling away of protected places for immigrants has fueled fears among health care workers that Immigration and Customs Enforcement (ICE) agents will arrest patients in or around hospitals. In January, the Trump administration rescinded a Biden-era policy that protected certain areas like churches, schools and hospitals from immigration enforcement. And lawmakers in at least one state have introduced legislation aimed at making it easier for ICE to make arrests in hospitals. As the Department of Homeland Security (DHS) seeks to ramp up ICE raids at hotels, restaurants, farms and other sites, nurses worry their workplace could be next. 'We were all worried about what this meant,' Michael Kennedy, a nurse at a University of California, San Diego health facility located very near the U.S.-Mexico border, said of the policy changes under Trump. 'As we've seen these immigration raids ramp up, our first thought is about our patients and what that means for them.' ICE agents made a record number of migrant arrests in a single day this month and have appeared outside of courthouses in Seattle and stores in the New York City area. The agency's workplace raids in Los Angeles spurred days of protests, which in turn prompted a heavy-handed response from the Trump administration. Sandy Reding is a nurse at a hospital in Bakersfield, Calif., which serves communities of farm workers and employs a diverse staff. 'There is a lot of concern [about] ICE agents showing up with FBI or with the military, because we've seen a lot of reports on TV, and we have reports in our area where this is happening as well,' she said. Reding and her fellow nurses, she said, are also worried that the news of increased ICE raids will deter some patients from coming to the hospital to seek care. 'What we are going to see is a large burden on communities and hospitals if people delay care,' Reding said. 'And there are worse outcomes.' Nancy Hagan, an intensive care unit nurse at Maimonides Medical Center in New York City, said those concerns have come to fruition at her hospital. In May, she said, an immigrant New Yorker had appendicitis but waited too long to go to the emergency room. Their appendix burst, spreading infected tissue and bacteria to other organs, which ultimately killed them. 'Once patients hear that a hospital is no longer a safe place for them to go, they are afraid to come to the hospital,' she said. Hagan, a Haitian immigrant, added that she and her colleagues, who work at hospitals across the city, have noticed that emergency rooms appear to be emptier in recent months. Kennedy, the nurse in San Diego, said the Level 1 trauma center, which is typically packed, has been emptier than usual. He admitted the decline in patient visits could be seasonally related, but he said he believes that the possibility of ICE agents arresting immigrants is having a 'chilling effect.' 'I can't see how this doesn't affect our patients' willingness to seek care,' he said. 'I'm willing to bet that a lot of people are delaying care because they're afraid.' ICE did not get back to The Hill in response to questions on whether agents have arrested people in or around hospitals, or if there are plans to do so. DHS announced in January that it had rescinded former President Biden's guidelines on immigration enforcement at 'sensitive locations' that were first issued under former President Obama. 'The Trump Administration will not tie the hands of our brave law enforcement, and instead trusts them to use common sense,' a DHS spokesperson said at the time. The National Immigration Law Center said that while immigrants no longer have special protections at hospitals and other 'sensitive locations,' they still have basic rights. 'Instead, individuals will need to rely on basic constitutional protections in these spaces,' it said in a fact sheet. 'Specifically, the Fourth Amendment protects all individuals from unreasonable searches and seizures, and the Fifth Amendment ensures the right to remain silent when confronted by law enforcement.' The Emergency Medicine Residents' Association has distributed a flyer with step-by-step guidance for health care workers on dealing with ICE agents if they do enter hospitals. Copyright 2025 Nexstar Media, Inc. All rights reserved. This material may not be published, broadcast, rewritten, or redistributed.
